Groundbreaking Gene Therapy Solves Lily's Sickle Cell Disease

Groundbreaking Gene Therapy Solves Lily’s Sickle Cell Disease sewardsk3 Fri, 09/11/2026 - 15:42 Before coming to CHOP, Lily dealt with consistent “acute events” which always forced the family to visit their local hospital. Not long after she was born, Lily was diagnosed with sickle cell disease . A group of inherited blood disorders affecting the shape and behavior of red blood cells, sickle cell disease tends to be characterized by anemia, pain and a whole host of other complications.